Genes associated with “Charcot-Marie-Tooth

109 genes foundOpen Targets: Charcot-Marie-Tooth disease type 26971 ClinVar P/LP variants
How are genes scored? (0–100 composite)
-5–15
ClinGen
0–15
HPO Freq
0–15
Open Targets
0–12
Phen2Gene
0–10
ClinVar
0–8
Constraint
0–8
Dosage
0–8
OMIM CS
0–8
PanelApp
0–5
OMIM
0–5
G2P
0–4
Breadth
Tiers:Strong Candidates (≥20)Consider (≥8)Possible (≥3)
Evidence dots:
HPOClinVarPhen2GeneOpen TargetsPanelApp
hover for details

Strong Candidates

34 genes
47
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
11
OT Score
-
2
MORC2

MORC family CW-type zinc finger 2

42
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
4
OT Score
0.83
3
MPZ

myelin protein zero

39
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
19
OT Score
0.86
4
GDAP1

ganglioside induced differentiation associated protein 1

39
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
11
OT Score
0.86
5
NEFL

neurofilament light chain

39
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
6
OT Score
0.85
6
AARS1

alanyl-tRNA synthetase 1

38
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
16
OT Score
0.81
7
LRSAM1

leucine rich repeat and sterile alpha motif containing 1

38
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
12
OT Score
0.80
8
MME

membrane metalloendopeptidase

38
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
10
OT Score
0.77
9
DNM2

dynamin 2

36
score
ClinGen: DefinitiveGTR ↑
Frequency
-
P/LP Variants
3
OT Score
0.55
35HSPB1
Def

heat shock protein family B (small) member 1

34DYNC1H1
Def

dynein cytoplasmic 1 heavy chain 1

33NEFH
Def

neurofilament heavy chain

31MFN2
Def

mitofusin 2

30LMNA
DefSF

lamin A/C

30ATP1A1
Mod

ATPase Na+/K+ transporting subunit alpha 1

28FGD4
Def
28SBF2
Def
27RAB7A
Def

RAB7A, member RAS oncogene family

27GARS1
Def

glycyl-tRNA synthetase 1

27HINT1
Def

histidine triad nucleotide binding protein 1

26IGHMBP2
Def

immunoglobulin mu DNA binding protein 2

26SPG11
Def

SPG11 vesicle trafficking associated, spatacsin

26VCP
Def

valosin containing protein

25FIG4
Def
25GJB1
Def
25PRX
Def
25NAGLU
Def

N-acetyl-alpha-glucosaminidase

24TRPV4
Def

transient receptor potential cation channel subfamily V member 4

23MPV17
Def

mitochondrial inner membrane protein MPV17

23INF2
Def
22BSCL2
Def

BSCL2 lipid droplet biogenesis associated, seipin

tripartite motif containing 2

22DNAJB2
Def

DnaJ heat shock protein family (Hsp40) member B2

21EGR2
Def

Consider

35 genes
19PNKP
Def

polynucleotide kinase 3'-phosphatase

19DHTKD1
Def

dehydrogenase E1 and transketolase domain containing 1

18MARS1
Lim

methionyl-tRNA synthetase 1

18KIF1B
No

kinesin family member 1B

16MTMR2
Def
16PLEKHG5
Def
16SH3TC2
Def
15KIF5A
Def

kinesin family member 5A

14HSPB8
Def

heat shock protein family B (small) member 8

14PRPS1
Def
14GNB4
Mod
13CHCHD10
Def

CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2JJ; CMT2JJ

CHARCOT-MARIE-TOOTH DISEASE, X-LINKED DOMINANT, 1; CMTX1

Charcot-Marie-Tooth neuropathy, X-linked recessive, 2

Charcot-Marie-Tooth neuropathy, X-linked recessive, 3

CHARCOT-MARIE-TOOTH DISEASE, X-LINKED DOMINANT, 6; CMTX6

13GAN
Def
13JAG1
Def
13SURF1
Def
12LITAF
Mod
12DARS2
Def
12HARS1
Ref

histidyl-tRNA synthetase 1

10PMP2
Mod
9AIFM1
Def
9POLR3B
Def
9MED25
Dis

mediator complex subunit 25

DDB1 and CUL4 associated factor 8

Possible

35 genes — click to expand
7KIF1A
Def

kinesin family member 1A

7BAG3
DefSF
7COX10
Def
7MCM3AP
Def
7ATP7A
Def

ATPase copper transporting alpha

6SLC5A7
Mod

solute carrier family 5 member 7

CHARCOT-MARIE-TOOTH DISEASE, DEMYELINATING, TYPE 1B; CMT1B

CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2A1; CMT2A1

CHARCOT-MARIE-TOOTH DISEASE, AXONAL, AUTOSOMAL DOMINANT, TYPE 2A2A; CMT2A2A

CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2B1; CMT2B1

CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2B2; CMT2B2

CHARCOT-MARIE-TOOTH DISEASE, AXONAL, TYPE 2K; CMT2K

CHARCOT-MARIE-TOOTH DISEASE, DEMYELINATING, TYPE 4B1; CMT4B1

CHARCOT-MARIE-TOOTH DISEASE, DEMYELINATING, TYPE 4B2; CMT4B2

CHARCOT-MARIE-TOOTH DISEASE, DEMYELINATING, TYPE 4H; CMT4H

CHARCOT-MARIE-TOOTH DISEASE, DOMINANT INTERMEDIATE B; CMTDIB

NEURONOPATHY, DISTAL HEREDITARY MOTOR, AUTOSOMAL DOMINANT 3; HMND3

NEURONOPATHY, DISTAL HEREDITARY MOTOR, AUTOSOMAL DOMINANT 7; HMND7

NEUROPATHY, HEREDITARY MOTOR AND SENSORY, TYPE VIA, WITH OPTIC ATROPHY; HMSN6A

heat shock protein family B (small) member 3

Data aggregated from HPO/Monarch, ClinVar, OMIM (phenotypes + clinical synopsis), Open Targets, PanelApp, Phen2Gene, and Gene2Phenotype. Click a gene to view full details.