VPS13A

Chr 9

vacuolar protein sorting 13 homolog A

Also known as: BLTP5A, CHAC, CHOREIN

The protein encoded by this gene may control steps in the cycling of proteins through the trans-Golgi network to endosomes, lysosomes and the plasma membrane. Mutations in this gene cause the autosomal recessive disorder, chorea-acanthocytosis. Alternative splicing of this gene results in multiple transcript variants. [provided by RefSeq, Jul 2008]

GeneReviewsResearchGenerating clinical summary…

Primary Disease Associations & Inheritance

UniProtChoreoacanthocytosis
0
Active trials
37
Pubs (1 yr)
P/LP submissions
P/LP missense
0.48
LOEUF
Mechanism
📖
GeneReview available — VPS13A
Authoritative clinical overview · Recommended first read
Open GeneReview ↗
Some data sources returned errors (1)

omim: Error: OMIM fetch failed: 429

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint?
0.48LOEUF
pLI 0.000
Z-score 7.34
OE 0.40 (0.320.48)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint?
1.76Z-score
OE missense 0.88 (0.840.92)
1408 obs / 1606.3 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios?
LoF OE?0.40 (0.320.48)
00.351.4
Missense OE?0.88 (0.840.92)
00.61.4
Synonymous OE?0.99
01.21.6
LoF obs/exp: 68 / 171.9Missense obs/exp: 1408 / 1606.3Syn Z: 0.13

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

VPS13A · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →