VKORC1

Chr 16ARAD

vitamin K epoxide reductase complex subunit 1

Also known as: EDTP308, MST134, MST576, VKCFD2, VKOR

The protein is the catalytic subunit of vitamin K epoxide reductase complex, which reduces inactive vitamin K 2,3-epoxide to active vitamin K required for gamma-carboxylation of clotting factors and normal blood coagulation. Mutations cause combined deficiency of vitamin K-dependent clotting factors type 2, presenting with bleeding disorders that can manifest in infancy or childhood. The condition follows autosomal recessive inheritance.

OMIMResearchSummary from RefSeq, UniProt
MultiplemechanismAR/ADLOEUF 1.022 OMIM phenotypes
Clinical SummaryVKORC1
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Gene-Disease Validity (ClinGen)
vitamin K-dependent clotting factors, combined deficiency of, type 2 · ARModerate

Moderate evidence — consider for supplementary testing

Population Constraint (gnomAD)
Constrained for loss-of-function variants (OE-LoF 0.32) despite low pLI — interpret in context.
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.02LOEUF
pLI 0.162
Z-score 1.55
OE 0.32 (0.131.02)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.31Z-score
OE missense 0.91 (0.761.09)
85 obs / 93.3 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.32 (0.131.02)
00.351.4
Missense OE0.91 (0.761.09)
00.61.4
Synonymous OE0.90
01.21.6
LoF obs/exp: 2 / 6.2Missense obs/exp: 85 / 93.3Syn Z: 0.54
DN
0.76top 25%
GOF
0.6541th %ile
LOF
0.2092th %ile

This gene has evidence for multiple mechanisms of pathogenicity (dominant-negative and gain-of-function). Both the Badonyi & Marsh prediction and the broader genomic evidence point to dominant-negative as the predominant mechanism. Different variants in this gene may act through different mechanisms — interpret in context of the specific variant.

DNprediction above median · 1 literature citation
GOFprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Literature Evidence

DNAn inactive mutant (VKORC1(C132A/C135A)) was dominant negative in heterodimers with wild type VKORC1, resulting in decreased KO reduction in cells and carboxylation in vitro.PMID:23918929

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

VKORC1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
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Full-Text Mentions
NLP-detected gene mentions in article bodies · via PubTator3
PubTator3
Top 5 full-text resultsSearch PubTator3 ↗