UPF2

Chr 10

UPF2 regulator of nonsense mediated mRNA decay

Also known as: HUPF2, RENT2, smg-3

UPF2 encodes a protein essential for nonsense-mediated mRNA decay (NMD), a cellular quality control mechanism that degrades mRNAs containing premature stop codons by forming surveillance complexes with UPF1 and UPF3 proteins. Mutations cause autosomal recessive intellectual disability with microcephaly and seizures, typically presenting in early childhood. This gene is extremely intolerant to loss-of-function mutations, reflecting its critical role in mRNA surveillance and cellular homeostasis.

Summary from RefSeq, UniProt
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0
Active trials
14
Pubs (1 yr)
18
P/LP submissions
0%
P/LP missense
0.10
LOEUF· LoF intol.
LOF
Mechanism· predicted
Clinical SummaryUPF2
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
18 unique Pathogenic / Likely Pathogenic· 135 VUS of 199 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Dual constrained — LoF & missense intolerant
LoF Constraint
0.10LOEUF
pLI 1.000
Z-score 7.15
OE 0.03 (0.010.10)
Highly constrained

Among the most LoF-intolerant genes (~top 3%)

Missense Constraint
3.19Z-score
OE missense 0.65 (0.600.71)
438 obs / 670.6 exp
Constrained

Highly missense-constrained (top ~0.1%)

Observed / Expected Ratios
LoF OE0.03 (0.010.10)
00.351.4
Missense OE0.65 (0.600.71)
00.61.4
Synonymous OE1.04
01.21.6
LoF obs/exp: 2 / 63.4Missense obs/exp: 438 / 670.6Syn Z: -0.44
DN
0.2898th %ile
GOF
0.3391th %ile
LOF
0.75top 10%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · LOEUF 0.10

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

199 submitted variants in ClinVar

Classification Summary

Pathogenic18
VUS135
Likely Benign10
Benign8
18
Pathogenic
135
VUS
10
Likely Benign
8
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
1
0
17
0
18
Likely Pathogenic
0
0
0
0
0
VUS
0
125
10
0
135
Likely Benign
0
2
5
3
10
Benign
0
0
4
4
8
Total1127367171

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

UPF2 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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