UBR5

Chr 8AD

ubiquitin protein ligase E3 component n-recognin 5

Also known as: DD5, EDD, EDD1, HYD, NEDSBH

UBR5 encodes an E3 ubiquitin-protein ligase that targets specific proteins for degradation through the ubiquitin-proteasome system, playing critical roles in protein quality control, DNA damage response, and transcriptional regulation. Mutations cause autosomal dominant neurodevelopmental disorder with speech delay and behavioral abnormalities. This gene is highly constrained against loss-of-function variants (pLI=1, LOEUF=0.073), indicating that functional copies are essential for normal development.

Summary from RefSeq, OMIM, UniProt
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Primary Disease Associations & Inheritance

Neurodevelopmental disorder with speech delay and behavioral abnormalitiesMIM #621372
AD
0
Active trials
43
Pubs (1 yr)
8
P/LP submissions
38%
P/LP missense
0.07
LOEUF· LoF intol.
LOF
Mechanism· G2P
Clinical SummaryUBR5
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
8 unique Pathogenic / Likely Pathogenic· 152 VUS of 300 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Dual constrained — LoF & missense intolerant
LoF Constraint
0.07LOEUF
pLI 1.000
Z-score 11.34
OE 0.04 (0.020.07)
Highly constrained

Among the most LoF-intolerant genes (~top 3%)

Missense Constraint
6.21Z-score
OE missense 0.55 (0.520.58)
843 obs / 1525.0 exp
Constrained

Extremely missense-constrained (top ~0.01%)

Observed / Expected Ratios
LoF OE0.04 (0.020.07)
00.351.4
Missense OE0.55 (0.520.58)
00.61.4
Synonymous OE0.94
01.21.6
LoF obs/exp: 6 / 161.6Missense obs/exp: 843 / 1525.0Syn Z: 1.01
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
moderateUBR5-related neurodevelopmental disorderLOFAD
DN
0.20100th %ile
GOF
0.1799th %ile
LOF
0.88top 5%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · LOEUF 0.07

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

300 submitted variants in ClinVar

Classification Summary

Pathogenic8
VUS152
Likely Benign37
Benign5
8
Pathogenic
152
VUS
37
Likely Benign
5
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
1
3
4
0
8
Likely Pathogenic
0
0
0
0
0
VUS
0
149
3
0
152
Likely Benign
0
6
7
24
37
Benign
0
0
1
4
5
Total11581528202

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

UBR5 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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