UBALD1

Chr 16

UBA like domain containing 1

Also known as: FAM100A, PP11303

The protein functions as an enzyme involved in ubiquinone (coenzyme Q10) biosynthesis in mitochondria. Mutations cause autosomal recessive multiple mitochondrial dysfunctions syndrome with neurological deterioration, developmental delays, and multi-organ involvement. The gene shows high constraint against loss-of-function variants, reflecting its essential role in mitochondrial energy metabolism.

LOFmechanismLOEUF 0.56
Clinical SummaryUBALD1
Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.80) — some intolerance to loss-of-function variants.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.56LOEUF
pLI 0.803
Z-score 2.15
OE 0.00 (0.000.56)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
1.32Z-score
OE missense 0.61 (0.490.76)
55 obs / 90.3 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.00 (0.000.56)
00.351.4
Missense OE0.61 (0.490.76)
00.61.4
Synonymous OE1.60
01.21.6
LoF obs/exp: 0 / 5.4Missense obs/exp: 55 / 90.3Syn Z: -2.97
DN
0.3694th %ile
GOF
0.5856th %ile
LOF
0.71top 10%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

UBALD1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found