TKTL1

Chr X

transketolase like 1

Also known as: TKR, TKT2

The protein is a transketolase enzyme that catalyzes the transfer of two-carbon ketol groups between sugar phosphates, linking the pentose phosphate pathway with glycolysis through conversion of sedoheptulose 7-phosphate and glyceraldehyde 3-phosphate to ribose 5-phosphate and xylulose 5-phosphate. Mutations may cause Wernicke-Korsakoff syndrome, though the inheritance pattern is not established from the available data. The extremely high pLI score (0.999) and low LOEUF score (0.142) indicate this gene is highly intolerant to loss-of-function variants, suggesting haploinsufficiency as a likely pathogenic mechanism.

OMIMResearchSummary from RefSeq, UniProt
LOEUF 0.14
Clinical SummaryTKTL1
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.14LOEUF
pLI 0.999
Z-score 4.25
OE 0.00 (0.000.14)
Highly constrained

Among the most LoF-intolerant genes (~top 3%)

Missense Constraint
-0.85Z-score
OE missense 1.14 (1.041.26)
309 obs / 269.9 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.00 (0.000.14)
00.351.4
Missense OE1.14 (1.041.26)
00.61.4
Synonymous OE1.35
01.21.6
LoF obs/exp: 0 / 21.1Missense obs/exp: 309 / 269.9Syn Z: -2.82

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

TKTL1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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