SPECC1

Chr 17

sperm antigen with calponin homology and coiled-coil domains 1

Also known as: CYTSB, HCMOGT-1, HCMOGT1, NSP, NSP5

The SPECC1 protein is a nuclear-localized member of the cytospin-A family that is highly constrained against loss-of-function variants. Mutations cause Opitz G/BBB syndrome, an autosomal dominant disorder characterized by midline developmental defects including hypertelorism, cleft lip/palate, and genitourinary abnormalities. The gene's high constraint (pLI ~0.0009, LOEUF 0.49) reflects its critical role in normal midline development during embryogenesis.

OMIMResearchSummary from RefSeq
DNmechanismLOEUF 0.49
Clinical SummarySPECC1
Population Constraint (gnomAD)
Constrained for loss-of-function variants (OE-LoF 0.32) despite low pLI — interpret in context.
📋
ClinVar Variants
16 unique Pathogenic / Likely Pathogenic· 2 VUS of 18 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.49LOEUF
pLI 0.001
Z-score 4.23
OE 0.32 (0.210.49)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
-0.19Z-score
OE missense 1.02 (0.951.09)
619 obs / 606.0 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.32 (0.210.49)
00.351.4
Missense OE1.02 (0.951.09)
00.61.4
Synonymous OE1.14
01.21.6
LoF obs/exp: 14 / 44.4Missense obs/exp: 619 / 606.0Syn Z: -1.70
DN
0.6550th %ile
GOF
0.5563th %ile
LOF
0.4331th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

18 submitted variants in ClinVar

Classification Summary

Pathogenic16
VUS2
16
Pathogenic
2
VUS

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories· variant type breakdown unavailable

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
16
Likely Pathogenic
0
VUS
2
Likely Benign
0
Benign
0
Total18

Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

SPECC1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
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