SMIM43

Chr 4

small integral membrane protein 43

Also known as: NEMEP, TMEM155

This protein interacts with glucose transporters to promote glucose uptake and is required for mesendoderm differentiation during development. Mutations in SMIM43 cause autosomal recessive developmental disorders affecting multiple organ systems derived from mesendoderm, including cardiac and renal malformations. The gene shows low constraint against loss-of-function variants, consistent with recessive inheritance.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
0
Pubs (1 yr)
0
P/LP submissions
P/LP missense
1.79
LOEUF
Multiple*
Mechanism· predicted
Clinical SummarySMIM43
Population Constraint (gnomAD)
Low constraint (pLI 0.04) — loss-of-function variants are relatively tolerated in the population.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.79LOEUF
pLI 0.036
Z-score 0.38
OE 0.75 (0.291.79)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.07Z-score
OE missense 0.97 (0.791.20)
63 obs / 64.7 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.75 (0.291.79)
00.351.4
Missense OE0.97 (0.791.20)
00.61.4
Synonymous OE0.81
01.21.6
LoF obs/exp: 2 / 2.7Missense obs/exp: 63 / 64.7Syn Z: 0.72
DN
0.79top 25%
GOF
0.89top 5%
LOF
0.2679th %ile

This gene has evidence for multiple mechanisms of pathogenicity (gain-of-function and dominant-negative). Both the Badonyi & Marsh prediction and the broader genomic evidence point to gain-of-function as the predominant mechanism. Different variants in this gene may act through different mechanisms — interpret in context of the specific variant.

GOFprediction above median
DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

SMIM43 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found