SKIDA1

Chr 10

SKI/DACH domain containing 1

Also known as: C10orf140, DLN-1

The protein functions as a DNA-binding transcription factor that regulates gene expression through RNA polymerase II. Mutations cause autosomal recessive intellectual disability with variable additional features including seizures and developmental delays. This gene is highly constrained against loss-of-function variants (pLI 0.99, LOEUF 0.25), indicating that complete loss of protein function is likely pathogenic.

Summary from RefSeq
Research Assistant →
0
Active trials
5
Pubs (1 yr)
10
P/LP submissions
0%
P/LP missense
0.25
LOEUF· LoF intol.
LOF
Mechanism· predicted
Clinical SummarySKIDA1
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 0.99). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
10 unique Pathogenic / Likely Pathogenic· 162 VUS of 194 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.25LOEUF
pLI 0.992
Z-score 3.81
OE 0.05 (0.020.25)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
1.16Z-score
OE missense 0.84 (0.760.92)
333 obs / 398.0 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.05 (0.020.25)
00.351.4
Missense OE0.84 (0.760.92)
00.61.4
Synonymous OE1.06
01.21.6
LoF obs/exp: 1 / 18.8Missense obs/exp: 333 / 398.0Syn Z: -0.61
DN
0.2897th %ile
GOF
0.2895th %ile
LOF
0.84top 5%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · LOEUF 0.25

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

194 submitted variants in ClinVar

Classification Summary

Pathogenic9
Likely Pathogenic1
VUS162
Likely Benign12
Benign5
9
Pathogenic
1
Likely Pathogenic
162
VUS
12
Likely Benign
5
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
9
0
9
Likely Pathogenic
0
0
1
0
1
VUS
0
158
4
0
162
Likely Benign
0
6
3
3
12
Benign
0
2
3
0
5
Total0166203189

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

SKIDA1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC