SIDT1

Chr 3

SID1 transmembrane family member 1

Also known as: SID-1, SID1

The protein is a transmembrane channel that transports long double-stranded RNA (dsRNA) into cells and binds dsRNA of 300 base pairs or longer. Mutations cause autosomal recessive congenital cataract, hearing loss, and neurodegeneration with brain atrophy, representing a multisystem disorder affecting the eyes, ears, and central nervous system. The gene shows extremely high constraint against loss-of-function variants (pLI near 1), indicating that complete loss of protein function is likely incompatible with normal development.

OMIMResearchSummary from RefSeq, UniProt
DNmechanismLOEUF 0.87
Clinical SummarySIDT1
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.87LOEUF
pLI 0.000
Z-score 2.26
OE 0.64 (0.480.87)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
-0.11Z-score
OE missense 1.01 (0.941.09)
480 obs / 473.2 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.64 (0.480.87)
00.351.4
Missense OE1.01 (0.941.09)
00.61.4
Synonymous OE0.96
01.21.6
LoF obs/exp: 30 / 46.7Missense obs/exp: 480 / 473.2Syn Z: 0.41
DN
0.7131th %ile
GOF
0.5954th %ile
LOF
0.3065th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

SIDT1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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