SIAH1

Chr 16AD

siah E3 ubiquitin protein ligase 1

Also known as: BURHAS, SIAH1A

The protein is an E3 ubiquitin ligase that mediates ubiquitination and subsequent proteasomal degradation of target proteins involved in apoptosis, transcription regulation, cell cycle control, and other cellular processes. Mutations cause Buratti-Harel syndrome, which follows autosomal dominant inheritance. The gene is highly constrained against loss-of-function variants (LOEUF = 0.499), suggesting intolerance to protein-disrupting mutations.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismADLOEUF 0.501 OMIM phenotype
Clinical SummarySIAH1
Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.70) — some intolerance to loss-of-function variants.
📋
ClinVar Variants
34 unique Pathogenic / Likely Pathogenic· 38 VUS of 87 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Missense constrained — critical functional residues
LoF Constraint
0.50LOEUF
pLI 0.699
Z-score 2.77
OE 0.16 (0.060.50)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
3.23Z-score
OE missense 0.33 (0.270.41)
61 obs / 184.3 exp
Constrained

Highly missense-constrained (top ~0.1%)

Observed / Expected Ratios
LoF OE0.16 (0.060.50)
00.351.4
Missense OE0.33 (0.270.41)
00.61.4
Synonymous OE1.15
01.21.6
LoF obs/exp: 2 / 12.6Missense obs/exp: 61 / 184.3Syn Z: -1.00
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
strongSIAH1-related neurodevelopmental disorderOTHERAD
DN
0.4488th %ile
GOF
0.3689th %ile
LOF
0.67top 25%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · 24% of P/LP variants are LoF · LOEUF 0.50

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

87 submitted variants in ClinVar

Classification Summary

Pathogenic19
Likely Pathogenic15
VUS38
Likely Benign6
Benign2
Conflicting1
19
Pathogenic
15
Likely Pathogenic
38
VUS
6
Likely Benign
2
Benign
1
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
4
15
0
19
Likely Pathogenic
8
7
0
0
15
VUS
5
29
4
0
38
Likely Benign
0
0
0
6
6
Benign
0
0
0
2
2
Conflicting
1
Total134019881

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

SIAH1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
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