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SCAX1

Chr XXLR

spinocerebellar ataxia, X-linked 1

Also known as: CLA2, OPCA

The protein function for SCAX1 is not well-characterized in the provided information. Mutations cause X-linked recessive spinocerebellar ataxia affecting the cerebellum and coordination. The question mark in the OMIM phenotype designation indicates this is a provisional gene-disease association that requires further validation.

OMIMResearchSummary from OMIM
XLR1 OMIM phenotype
Some data sources returned errors (2)

ensembl: Error: Ensembl fetch failed: 400 for https://rest.ensembl.org/lookup/symbol/homo_sapiens/SCAX1?content-type=application/json&expand=1

gnomad: Error: Gene not found

Population Genetics & Constraint

Constraint data not available from gnomAD.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

SCAX1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Key Publications
Landmark & review papers · by relevance
PubMed
Top 1 results · since 2015Search PubMed ↗