RPUSD3

Chr 3

RNA pseudouridine synthase D3

This gene encodes a pseudouridine synthase that catalyzes pseudouridylation of specific mitochondrial mRNAs and participates in mitochondrial ribosome biogenesis by modifying 16S rRNA. Mutations cause mitochondrial disorders with defects in mitochondrial protein synthesis, typically presenting in early childhood with multisystem involvement including neurological, cardiac, and metabolic features. The gene shows minimal constraint against loss-of-function variants (pLI near 0), and inheritance pattern varies depending on the specific mitochondrial disorder but typically follows autosomal recessive inheritance.

OMIMResearchSummary from RefSeq, UniProt
LOEUF 1.10
Clinical SummaryRPUSD3
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
49 unique Pathogenic / Likely Pathogenic· 72 VUS of 144 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.10LOEUF
pLI 0.000
Z-score 1.24
OE 0.69 (0.451.10)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
-0.50Z-score
OE missense 1.10 (0.981.23)
217 obs / 197.1 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.69 (0.451.10)
00.351.4
Missense OE1.10 (0.981.23)
00.61.4
Synonymous OE1.10
01.21.6
LoF obs/exp: 13 / 18.8Missense obs/exp: 217 / 197.1Syn Z: -0.75

ClinVar Variant Classifications

144 submitted variants in ClinVar

Classification Summary

Pathogenic44
Likely Pathogenic5
VUS72
Likely Benign5
44
Pathogenic
5
Likely Pathogenic
72
VUS
5
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
44
0
44
Likely Pathogenic
0
2
3
0
5
VUS
1
53
18
0
72
Likely Benign
0
3
1
1
5
Benign
0
0
0
0
0
Total158661126

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

RPUSD3 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found