RFLNB

Chr 17

refilin B

Also known as: CFM1, FAM101B

The RFLNB protein regulates the perinuclear actin network and nuclear shape through filamin binding and plays an essential role in cartilaginous skeletal element formation. Mutations cause autosomal recessive spondylocarpotarsal synostosis syndrome, characterized by vertebral fusions and joint abnormalities affecting the skeletal system. The gene shows moderate tolerance to loss-of-function variants based on population genetics data.

OMIMResearchSummary from RefSeq, UniProt
GOFmechanism
Clinical SummaryRFLNB
📋
ClinVar Variants
58 unique Pathogenic / Likely Pathogenic· 44 VUS of 110 total submissions
Some data sources returned errors (1)

gnomad: TimeoutError: The operation was aborted due to timeout

Population Genetics & Constraint

Constraint data not available from gnomAD.

DN
0.5673th %ile
GOF
0.74top 25%
LOF
0.4332th %ile

The highest-scoring mechanism for this gene is gain-of-function.

GOFprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

110 submitted variants in ClinVar

Classification Summary

Pathogenic53
Likely Pathogenic5
VUS44
Likely Benign7
Conflicting1
53
Pathogenic
5
Likely Pathogenic
44
VUS
7
Likely Benign
1
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories· variant type breakdown unavailable

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
53
Likely Pathogenic
5
VUS
44
Likely Benign
7
Benign
0
Conflicting
1
Total110

Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

RFLNB · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
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