RER1

Chr 1

retention in endoplasmic reticulum sorting receptor 1

The protein localizes to the Golgi apparatus and retrieves endoplasmic reticulum membrane proteins from the early Golgi compartment, facilitating gamma-secretase complex assembly. Mutations cause autosomal recessive neurodevelopmental disorder with epilepsy and brain atrophy, typically presenting in infancy or early childhood. The gene shows moderate constraint against loss-of-function variants (LOEUF 0.58), and the disorder primarily affects the central nervous system with seizures and developmental delays as prominent features.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
4
Pubs (1 yr)
133
P/LP submissions
0%
P/LP missense
0.58
LOEUF
DN
Mechanism· predicted
Clinical SummaryRER1
Population Constraint (gnomAD)
Constrained for loss-of-function variants (OE-LoF 0.22) despite low pLI — interpret in context.
📋
ClinVar Variants
126 unique Pathogenic / Likely Pathogenic· 45 VUS of 188 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.58LOEUF
pLI 0.379
Z-score 2.64
OE 0.22 (0.100.58)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.13Z-score
OE missense 0.46 (0.370.57)
55 obs / 120.7 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.22 (0.100.58)
00.351.4
Missense OE0.46 (0.370.57)
00.61.4
Synonymous OE1.20
01.21.6
LoF obs/exp: 3 / 13.5Missense obs/exp: 55 / 120.7Syn Z: -1.12
DN
0.74top 25%
GOF
0.5856th %ile
LOF
0.3746th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

188 submitted variants in ClinVar

Classification Summary

Pathogenic123
Likely Pathogenic3
VUS45
Likely Benign2
Benign1
123
Pathogenic
3
Likely Pathogenic
45
VUS
2
Likely Benign
1
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
123
0
123
Likely Pathogenic
0
0
3
0
3
VUS
0
9
36
0
45
Likely Benign
0
0
2
0
2
Benign
0
0
1
0
1
Total091650174

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

RER1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →