RBM8A

Chr 1AR

RNA binding motif protein 8A

Also known as: BOV-1A, BOV-1B, BOV-1C, C1DELq21.1, DEL1q21.1, MDS014, RBM8, TAR

The protein is a core component of the exon junction complex that marks splice sites on mature mRNAs and is required for pre-mRNA splicing, mRNA export, translation regulation, and nonsense-mediated decay. Mutations cause thrombocytopenia-absent radius (TAR) syndrome, which presents in infancy with severe bleeding due to low platelet counts and bilateral absence of the radius bones. TAR syndrome follows autosomal recessive inheritance and the gene shows moderate constraint against loss-of-function variants (LOEUF 0.564).

GeneReviewsOMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 0.561 OMIM phenotype
Clinical SummaryRBM8A
🧬
Gene-Disease Validity (ClinGen)
thrombocytopenia-absent radius syndrome · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.57) — some intolerance to loss-of-function variants.
📖
GeneReview available — RBM8A
Authoritative clinical overview · Recommended first read
Open GeneReview ↗

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.56LOEUF
pLI 0.573
Z-score 2.54
OE 0.18 (0.070.56)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.16Z-score
OE missense 0.43 (0.340.55)
49 obs / 113.9 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.18 (0.070.56)
00.351.4
Missense OE0.43 (0.340.55)
00.61.4
Synonymous OE0.87
01.21.6
LoF obs/exp: 2 / 11.2Missense obs/exp: 49 / 113.9Syn Z: 0.66

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

RBM8A · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →