PTCD3

Chr 2AR

pentatricopeptide repeat domain 3

Also known as: COXPD51, MRP-S39, mS39

The PTCD3 protein binds mitochondrial RNA and is essential for mitochondrial translation, which produces key components of the electron transport chain. Mutations cause combined oxidative phosphorylation deficiency 51, inherited in an autosomal recessive pattern. This mitochondrial disorder affects multiple organ systems due to impaired cellular energy production.

Summary from RefSeq, OMIM, UniProt
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Primary Disease Associations & Inheritance

Combined oxidative phosphorylation deficiency 51MIM #619057
AR
0
Active trials
3
Pubs (1 yr)
24
P/LP submissions
4%
P/LP missense
1.08
LOEUF
Mechanism
Clinical SummaryPTCD3
🧬
Gene-Disease Validity (ClinGen)
Leigh syndrome · ARLimited

Limited evidence — not for standalone diagnostic reporting

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
23 unique Pathogenic / Likely Pathogenic· 127 VUS of 216 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.08LOEUF
pLI 0.000
Z-score 1.10
OE 0.82 (0.641.08)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
-0.48Z-score
OE missense 1.07 (0.981.16)
394 obs / 368.1 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.82 (0.641.08)
00.351.4
Missense OE1.07 (0.981.16)
00.61.4
Synonymous OE1.08
01.21.6
LoF obs/exp: 38 / 46.1Missense obs/exp: 394 / 368.1Syn Z: -0.71

ClinVar Variant Classifications

216 submitted variants in ClinVar

Classification Summary

Pathogenic16
Likely Pathogenic7
VUS127
Likely Benign14
Benign3
Conflicting3
16
Pathogenic
7
Likely Pathogenic
127
VUS
14
Likely Benign
3
Benign
3
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
3
1
12
0
16
Likely Pathogenic
3
0
4
0
7
VUS
0
106
20
1
127
Likely Benign
0
8
5
1
14
Benign
0
1
1
1
3
Conflicting
3
Total6116423170

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

PTCD3 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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