PPEF1

Chr X

protein phosphatase with EF-hand domain 1

Also known as: PP7, PPEF, PPP7C, PPP7CA

This protein is a serine/threonine phosphatase with calcium-binding EF-hand motifs that functions in sensory neuron development and photoreceptor recovery or adaptation responses. Mutations cause autosomal recessive neurodevelopmental disorders affecting vision and neurological function. The gene is highly constrained against loss-of-function variants, indicating that functional copies are critical for normal development.

OMIMResearchSummary from RefSeq, UniProt
LOEUF 0.29
Clinical SummaryPPEF1
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 0.99). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
37 unique Pathogenic / Likely Pathogenic· 40 VUS of 200 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.29LOEUF
pLI 0.987
Z-score 4.22
OE 0.11 (0.050.29)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
1.94Z-score
OE missense 0.65 (0.570.74)
156 obs / 240.9 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.11 (0.050.29)
00.351.4
Missense OE0.65 (0.570.74)
00.61.4
Synonymous OE0.91
01.21.6
LoF obs/exp: 3 / 26.4Missense obs/exp: 156 / 240.9Syn Z: 0.68

ClinVar Variant Classifications

200 submitted variants in ClinVar

Classification Summary

Pathogenic36
Likely Pathogenic1
VUS40
Likely Benign8
Benign2
36
Pathogenic
1
Likely Pathogenic
40
VUS
8
Likely Benign
2
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
36
0
36
Likely Pathogenic
0
0
1
0
1
VUS
0
25
15
0
40
Likely Benign
0
6
0
2
8
Benign
0
0
0
2
2
Total03152487

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

PPEF1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC