POGLUT2

Chr 13

protein O-glucosyltransferase 2

Also known as: EP58, ERp58, KDEL1, KDELC1

This protein is an endoplasmic reticulum glucosyltransferase that modifies extracellular EGF repeats of proteins including NOTCH1, NOTCH3, and fibrillin proteins, potentially regulating Notch signaling and protein transport to the plasma membrane. Mutations cause autosomal recessive limb-girdle muscular dystrophy type R21, which presents with progressive muscle weakness affecting the shoulder and hip girdle muscles. The gene shows no constraint against loss-of-function variants, consistent with recessive inheritance where heterozygous carriers are typically unaffected.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
3
Pubs (1 yr)
99
P/LP submissions
0%
P/LP missense
0.99
LOEUF
DN
Mechanism· predicted
Clinical SummaryPOGLUT2
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
99 unique Pathogenic / Likely Pathogenic· 81 VUS of 193 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.99LOEUF
pLI 0.000
Z-score 1.61
OE 0.66 (0.450.99)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.02Z-score
OE missense 1.00 (0.901.10)
273 obs / 273.7 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.66 (0.450.99)
00.351.4
Missense OE1.00 (0.901.10)
00.61.4
Synonymous OE0.96
01.21.6
LoF obs/exp: 17 / 25.8Missense obs/exp: 273 / 273.7Syn Z: 0.30
DN
0.6647th %ile
GOF
0.6053th %ile
LOF
0.3162th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

193 submitted variants in ClinVar

Classification Summary

Pathogenic98
Likely Pathogenic1
VUS81
Likely Benign2
98
Pathogenic
1
Likely Pathogenic
81
VUS
2
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
98
0
98
Likely Pathogenic
0
0
1
0
1
VUS
0
74
7
0
81
Likely Benign
0
2
0
0
2
Benign
0
0
0
0
0
Total0761060182

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

POGLUT2 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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