PGM2L1

Chr 11AR

phosphoglucomutase 2 like 1

Also known as: BM32A, NEDHFS, PMMLP

PGM2L1 encodes a glucose 1,6-bisphosphate synthase that uses 1,3-bisphosphoglycerate as a phosphate donor with various 1-phosphate sugars as acceptors in glucose metabolism. Mutations cause a neurodevelopmental disorder with hypotonia, dysmorphic facies, and skin abnormalities that follows autosomal recessive inheritance. The gene shows high constraint against loss-of-function variants (LOEUF 0.498), indicating intolerance to inactivating mutations.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 0.501 OMIM phenotype
Clinical SummaryPGM2L1
Population Constraint (gnomAD)
Constrained for loss-of-function variants (OE-LoF 0.29) despite low pLI — interpret in context.
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.50LOEUF
pLI 0.026
Z-score 3.72
OE 0.29 (0.170.50)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.24Z-score
OE missense 0.65 (0.580.73)
214 obs / 328.2 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.29 (0.170.50)
00.351.4
Missense OE0.65 (0.580.73)
00.61.4
Synonymous OE0.86
01.21.6
LoF obs/exp: 9 / 31.5Missense obs/exp: 214 / 328.2Syn Z: 1.14
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
strongPGM2L1-related neurodevelopmental disorderLOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.6840th %ile
GOF
0.4776th %ile
LOF
0.2874th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

PGM2L1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
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