PEX7

Chr 6AR

peroxisomal biogenesis factor 7

Also known as: PBD9B, PTS2R, RCDP1, RD

Encodes the cytosolic receptor for peroxisomal matrix enzymes that contain peroxisome targeting signal 2 (PTS2), facilitating their import into peroxisomes. Mutations cause autosomal recessive peroxisome biogenesis disorders including rhizomelic chondrodysplasia punctata type 1 and peroxisome biogenesis disorder 9B through impaired import of peroxisomal matrix proteins. The pathogenic mechanism involves defective peroxisomal protein targeting, leading to multiple peroxisomal functional defects.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 1.422 OMIM phenotypes
Clinical SummaryPEX7
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Gene-Disease Validity (ClinGen)
peroxisome biogenesis disorder · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
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Clinical Trials
4 active or recruiting trials — potential therapeutic options may be available

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.42LOEUF
pLI 0.000
Z-score 0.14
OE 0.97 (0.671.42)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.50Z-score
OE missense 0.89 (0.781.02)
145 obs / 162.9 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.97 (0.671.42)
00.351.4
Missense OE0.89 (0.781.02)
00.61.4
Synonymous OE1.12
01.21.6
LoF obs/exp: 19 / 19.7Missense obs/exp: 145 / 162.9Syn Z: -0.75
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
definitivePEX7-related peroxisome biogenesis disorder complementation group 11LOFAR
definitivePEX7-related rhizomelic chondrodysplasia punctataLOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.6452th %ile
GOF
0.5170th %ile
LOF
0.4331th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

PEX7 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
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