PET100

Chr 19AR

PET100 cytochrome c oxidase chaperone

Also known as: C19orf79, MC4DN12

PET100 encodes a small protein essential for the maturation and assembly of mitochondrial complex IV (cytochrome c oxidase), which is part of the respiratory electron transport chain. Mutations cause mitochondrial complex IV deficiency with autosomal recessive inheritance, resulting in a mitochondrial respiratory chain disorder. The gene is not highly constrained against loss-of-function variants, consistent with its recessive inheritance pattern.

GeneReviewsOMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 1.821 OMIM phenotype
Clinical SummaryPET100
🧬
Gene-Disease Validity (ClinGen)
Leigh syndrome · ARModerate

Moderate evidence — consider for supplementary testing

2 total gene-disease associations curated

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📖
GeneReview available — PET100
Authoritative clinical overview · Recommended first read
Open GeneReview ↗

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.82LOEUF
pLI 0.000
Z-score -0.06
OE 1.03 (0.531.82)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
0.24Z-score
OE missense 0.90 (0.691.17)
38 obs / 42.4 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE1.03 (0.531.82)
00.351.4
Missense OE0.90 (0.691.17)
00.61.4
Synonymous OE0.54
01.21.6
LoF obs/exp: 5 / 4.9Missense obs/exp: 38 / 42.4Syn Z: 1.37
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
strongPET100-related mitochondrial complex IV deficiencyLOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.75top 25%
GOF
0.76top 25%
LOF
0.2483th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

PET100 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →