PCYT1B

Chr X

phosphate cytidylyltransferase 1B, choline

Also known as: CCTB, CTB

The protein catalyzes the rate-limiting step in the CDP-choline pathway for phosphatidylcholine biosynthesis, which is essential for cellular membrane formation. Mutations cause autosomal recessive cone-rod dystrophy with hearing loss, typically presenting in childhood with progressive visual impairment affecting both photoreceptor types and sensorineural deafness. This gene is highly constrained against loss-of-function variants, indicating its critical biological importance.

OMIMResearchSummary from RefSeq, UniProt
LOEUF 0.40
Clinical SummaryPCYT1B
Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.90) — some intolerance to loss-of-function variants.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.40LOEUF
pLI 0.897
Z-score 2.91
OE 0.09 (0.030.40)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.16Z-score
OE missense 0.48 (0.390.59)
65 obs / 135.8 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.09 (0.030.40)
00.351.4
Missense OE0.48 (0.390.59)
00.61.4
Synonymous OE1.09
01.21.6
LoF obs/exp: 1 / 11.8Missense obs/exp: 65 / 135.8Syn Z: -0.50

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

PCYT1B · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found