PCM1

Chr 8

pericentriolar material 1

Also known as: PTC4, RET/PCM-1

PCM1 encodes a component of centriolar satellites that is essential for centrosome assembly, localization of centrosomal proteins, anchoring microtubules to the centrosome, and cilium biogenesis. Mutations cause autosomal recessive primary microcephaly with intellectual disability and growth retardation, typically presenting in infancy with severe developmental delays. This gene is highly constrained against loss-of-function variants, reflecting its critical role in cellular organization and brain development.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
28
Pubs (1 yr)
13
P/LP submissions
0%
P/LP missense
0.58
LOEUF
Mechanism
Clinical SummaryPCM1
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
13 unique Pathogenic / Likely Pathogenic· 295 VUS of 400 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.58LOEUF
pLI 0.000
Z-score 5.02
OE 0.45 (0.350.58)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
-6.16Z-score
OE missense 1.56 (1.501.63)
1474 obs / 942.1 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.45 (0.350.58)
00.351.4
Missense OE1.56 (1.501.63)
00.61.4
Synonymous OE1.51
01.21.6
LoF obs/exp: 43 / 96.1Missense obs/exp: 1474 / 942.1Syn Z: -7.26

ClinVar Variant Classifications

400 submitted variants in ClinVar

Classification Summary

Pathogenic13
VUS295
Likely Benign25
13
Pathogenic
295
VUS
25
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
13
0
13
Likely Pathogenic
0
0
0
0
0
VUS
1
291
3
0
295
Likely Benign
0
18
3
4
25
Benign
0
0
0
0
0
Total1309194333

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

PCM1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Key Publications
Landmark & review papers · by relevance
PubMed
Top 5 results · since 2015Search PubMed ↗