PAFAH2

Chr 1

platelet activating factor acetylhydrolase 2

Also known as: HSD-PLA2

The encoded enzyme catalyzes the hydrolysis and inactivation of platelet-activating factor (PAF) and other short-chain phospholipids by removing acetyl groups at the sn-2 position. Biallelic mutations cause neurodevelopmental disorder with seizures and brain atrophy, inherited in an autosomal recessive pattern. This gene is not highly constrained against loss-of-function variants.

OMIMResearchSummary from RefSeq, UniProt
LOEUF 1.11
Clinical SummaryPAFAH2
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
5 unique Pathogenic / Likely Pathogenic· 74 VUS of 98 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.11LOEUF
pLI 0.000
Z-score 1.16
OE 0.73 (0.491.11)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
-0.12Z-score
OE missense 1.02 (0.921.14)
239 obs / 233.8 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.73 (0.491.11)
00.351.4
Missense OE1.02 (0.921.14)
00.61.4
Synonymous OE1.04
01.21.6
LoF obs/exp: 16 / 21.8Missense obs/exp: 239 / 233.8Syn Z: -0.26

ClinVar Variant Classifications

98 submitted variants in ClinVar

Classification Summary

Pathogenic5
VUS74
Likely Benign1
5
Pathogenic
74
VUS
1
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
5
0
5
Likely Pathogenic
0
0
0
0
0
VUS
0
70
4
0
74
Likely Benign
0
1
0
0
1
Benign
0
0
0
0
0
Total0719080

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

PAFAH2 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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