ODC1

Chr 2AD

ornithine decarboxylase 1

Also known as: BABS, NEDBA, NEDBIA, ODC

This protein catalyzes the rate-limiting step in polyamine biosynthesis, converting ornithine to putrescine, which is essential for cell proliferation and DNA replication. Mutations cause Bachmann-Bupp syndrome, an autosomal dominant condition affecting neurodevelopment and growth. The gene shows moderate constraint against loss-of-function variants (LOEUF 0.543), and detailed clinical information is available in GeneReviews.

GeneReviewsOMIMResearchSummary from RefSeq, OMIM, UniProt
GOFmechanismADLOEUF 0.541 OMIM phenotype
Clinical SummaryODC1
Population Constraint (gnomAD)
Constrained for loss-of-function variants (OE-LoF 0.26) despite low pLI — interpret in context.
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available
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GeneReview available — ODC1
Authoritative clinical overview · Recommended first read
Open GeneReview ↗

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.54LOEUF
pLI 0.170
Z-score 3.02
OE 0.26 (0.130.54)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
1.47Z-score
OE missense 0.75 (0.670.84)
209 obs / 277.8 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.26 (0.130.54)
00.351.4
Missense OE0.75 (0.670.84)
00.61.4
Synonymous OE1.12
01.21.6
LoF obs/exp: 5 / 19.4Missense obs/exp: 209 / 277.8Syn Z: -0.95
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
strongODC1-related neurodevelopmental disorderGOFAD
DN
0.7034th %ile
GOF
0.4875th %ile
LOF
0.3067th %ile

This gene has evidence for multiple mechanisms of pathogenicity (dominant-negative and gain-of-function). Both the Badonyi & Marsh prediction and the broader genomic evidence point to dominant-negative as the predominant mechanism. Different variants in this gene may act through different mechanisms — interpret in context of the specific variant.

DNprediction above median
GOF1 literature citation

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Literature Evidence

GOFGain-of-function variants in the ODC1 gene cause a syndromic neurodevelopmental disorder associated with macrocephaly, alopecia, dysmorphic features, and neuroimaging abnormalities.PMID:30475435

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

ODC1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
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