NEU2

Chr 2

neuraminidase 2

Also known as: SIAL2

NEU2 encodes a cytosolic sialidase enzyme that catalyzes the hydrolytic cleavage of terminal sialic acid residues from gangliosides, glycoproteins, and oligosaccharides, with preference for specific sialyl linkage positions. Mutations cause autosomal recessive sialidosis with neurodegeneration affecting the central nervous system. The gene shows minimal constraint against loss-of-function variants (pLI near zero, LOEUF 1.928), suggesting the associated phenotypes may be relatively mild or uncommon.

Summary from RefSeq, UniProt
Research Assistant →
1
Active trials
6
Pubs (1 yr)
33
P/LP submissions
0%
P/LP missense
1.93
LOEUF
Mechanism
Clinical SummaryNEU2
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
33 unique Pathogenic / Likely Pathogenic· 61 VUS of 99 total submissions
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.93LOEUF
pLI 0.000
Z-score -1.62
OE 1.52 (1.021.93)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
-0.02Z-score
OE missense 1.00 (0.901.12)
243 obs / 242.0 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE1.52 (1.021.93)
00.351.4
Missense OE1.00 (0.901.12)
00.61.4
Synonymous OE0.85
01.21.6
LoF obs/exp: 17 / 11.2Missense obs/exp: 243 / 242.0Syn Z: 1.26

ClinVar Variant Classifications

99 submitted variants in ClinVar

Classification Summary

Pathogenic32
Likely Pathogenic1
VUS61
Likely Benign5
32
Pathogenic
1
Likely Pathogenic
61
VUS
5
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
32
0
32
Likely Pathogenic
0
0
1
0
1
VUS
0
55
6
0
61
Likely Benign
0
5
0
0
5
Benign
0
0
0
0
0
Total06039099

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

NEU2 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
Open Research Assistant →
Key Publications
Landmark & review papers · by relevance
PubMed
Top 3 results · since 2015Search PubMed ↗