NAA10

Chr XX-linkedXLDXLR

N-alpha-acetyltransferase 10, NatA catalytic subunit

Also known as: ARD1, ARD1A, ARD1P, DXS707, LZMS, MAA, MCOPS1, NATD

The protein functions as the catalytic subunit of the major N-terminal acetyltransferase complex, transferring acetyl groups from acetyl-coenzyme A to the alpha-amino group of nascent polypeptides, a modification essential for normal cell function. Mutations cause Ogden syndrome and syndromic microphthalmia type 1, following X-linked inheritance patterns including dominant and recessive forms. The pathogenic mechanism involves disruption of this critical post-translational modification process affecting protein function.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismX-linked/XLD/XLRLOEUF 0.522 OMIM phenotypes
Clinical SummaryNAA10
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Gene-Disease Validity (ClinGen)
NAA10-related syndrome · XLDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.76) — some intolerance to loss-of-function variants.
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ClinVar Variants
205 unique Pathogenic / Likely Pathogenic· 81 VUS of 424 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.52LOEUF
pLI 0.762
Z-score 2.49
OE 0.11 (0.040.52)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.41Z-score
OE missense 0.33 (0.250.44)
33 obs / 101.2 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.11 (0.040.52)
00.351.4
Missense OE0.33 (0.250.44)
00.61.4
Synonymous OE1.06
01.21.6
LoF obs/exp: 1 / 9.1Missense obs/exp: 33 / 101.2Syn Z: -0.31

ClinVar Variant Classifications

424 submitted variants in ClinVar

Classification Summary

Pathogenic181
Likely Pathogenic24
VUS81
Likely Benign49
Benign30
Conflicting17
181
Pathogenic
24
Likely Pathogenic
81
VUS
49
Likely Benign
30
Benign
17
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
2
8
171
0
181
Likely Pathogenic
1
17
6
0
24
VUS
1
56
24
0
81
Likely Benign
1
4
24
20
49
Benign
0
1
22
7
30
Conflicting
17
Total58624727382

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

NAA10 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC