MTO1

Chr 6AR

mitochondrial tRNA translation optimization 1

Also known as: CGI-02, COXPD10

This nuclear gene encodes a mitochondrial protein that forms a complex with GTPBP3 to catalyze tRNA modifications essential for mitochondrial translation. Mutations cause combined oxidative phosphorylation deficiency 10, inherited in an autosomal recessive pattern. The gene is highly constrained against loss-of-function variants (pLI near 1, LOEUF 0.64), reflecting its critical role in mitochondrial function.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 0.641 OMIM phenotype
Clinical SummaryMTO1
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Gene-Disease Validity (ClinGen)
mitochondrial disease · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.64LOEUF
pLI 0.000
Z-score 3.25
OE 0.42 (0.280.64)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.65Z-score
OE missense 0.91 (0.830.99)
373 obs / 410.0 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.42 (0.280.64)
00.351.4
Missense OE0.91 (0.830.99)
00.61.4
Synonymous OE0.94
01.21.6
LoF obs/exp: 15 / 36.1Missense obs/exp: 373 / 410.0Syn Z: 0.54
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
definitiveMTO1-related infantile hypertrophic cardiomyopathy and lactic acidosisLOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.7326th %ile
GOF
0.5267th %ile
LOF
0.3550th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

MTO1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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