MDDGA4

Chr 9

fukutin

Also known as: CMD1X, FCMD, LGMD2M, LGMDR13, MDDGA4, MDDGB4, MDDGC4

The protein encoded by this gene is a putative transmembrane protein that is localized to the cis-Golgi compartment, where it may be involved in the glycosylation of alpha-dystroglycan in skeletal muscle. The encoded protein is thought to be a glycosyltransferase and could play a role in brain development. Defects in this gene are a cause of Fukuyama-type congenital muscular dystrophy (FCMD), Walker-Warburg syndrome (WWS), limb-girdle muscular dystrophy type 2M (LGMD2M), and dilated cardiomyopathy type 1X (CMD1X). Alternatively spliced transcript variants have been found for this gene. [provided by RefSeq, Nov 2010]

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ClinVar variants
0
Pathogenic / LP
pLI score
0
Active trials
Clinical SummaryMDDGA4
Some data sources returned errors (3)

ensembl: Error: Ensembl fetch failed: 400 for https://rest.ensembl.org/lookup/symbol/homo_sapiens/MDDGA4?content-type=application/json&expand=1

gnomad: Error: Gene not found

omim: Error: OMIM fetch failed: 429

Population Genetics & Constraint

Constraint data not available from gnomAD.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

MDDGA4 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

OMIM — Genotype-Phenotype

No OMIM entries found.

📖
GeneReview available — MDDGA4
Authoritative clinical overview · NCBI Bookshelf · Recommended first read
Open GeneReview ↗
Clinical Literature
Landmark / reviewRecent case evidence
Key Publications
Landmark & review papers · by relevance
PubMed
Syndromic Hydrocephalus.
Varagur K et al.·Neurosurg Clin N Am
2022Review
Dandy-Walker Malformation.
Society for Maternal-Fetal Medicine (SMFM) et al.·Am J Obstet Gynecol
2020Review
Walker-Warburg syndrome.
Vajsar J et al.·Orphanet J Rare Dis
2006Review
Walker-Warburg syndrome.
Suthar R et al.·Neurol India
2018Case report
Fukutin and alpha-dystroglycanopathies.
Toda T et al.·Acta Myol
2005Review
Walker-Warburg syndrome.
Agrawal S·BMJ Case Rep
2011Case report
Walker-Warburg Syndrome.
Khalaf SS et al.·J AAPOS
2006Case report
[Αlpha-dystroglycanopathy].
Toda T·Rinsho Shinkeigaku
2013
Top 10 resultsSearch PubMed ↗
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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