MANSC4

Chr 12

MANSC domain containing 4

Mannosyl-oligosaccharide glucosidase catalyzes the first step in N-linked glycoprotein processing by removing glucose residues from oligosaccharides in the endoplasmic reticulum. Biallelic mutations cause autosomal recessive intellectual disability with seizures and spasticity. The gene is highly constrained against loss-of-function variants, indicating intolerance to protein disruption.

0
Active trials
1
Pubs (1 yr)
33
P/LP submissions
0%
P/LP missense
1.88
LOEUF
Multiple*
Mechanism· predicted
Clinical SummaryMANSC4
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
33 unique Pathogenic / Likely Pathogenic· 40 VUS of 79 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.88LOEUF
pLI 0.000
Z-score -0.44
OE 1.21 (0.641.88)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
1.62Z-score
OE missense 0.66 (0.560.77)
115 obs / 175.3 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE1.21 (0.641.88)
00.351.4
Missense OE0.66 (0.560.77)
00.61.4
Synonymous OE0.76
01.21.6
LoF obs/exp: 6 / 5.0Missense obs/exp: 115 / 175.3Syn Z: 1.55
DN
0.6647th %ile
GOF
0.6444th %ile
LOF
0.3648th %ile

This gene has evidence for multiple mechanisms of pathogenicity (dominant-negative and gain-of-function). Both the Badonyi & Marsh prediction and the broader genomic evidence point to dominant-negative as the predominant mechanism. Different variants in this gene may act through different mechanisms — interpret in context of the specific variant.

DNprediction above median
GOFprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

79 submitted variants in ClinVar

Classification Summary

Pathogenic31
Likely Pathogenic2
VUS40
Likely Benign4
31
Pathogenic
2
Likely Pathogenic
40
VUS
4
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
31
0
31
Likely Pathogenic
0
0
2
0
2
VUS
0
37
3
0
40
Likely Benign
0
4
0
0
4
Benign
0
0
0
0
0
Total04136077

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

MANSC4 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Key Publications
Landmark & review papers · by relevance
PubMed
Top 1 results · since 2015Search PubMed ↗
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found