LMX1B

Chr 9AD

LIM homeobox transcription factor 1 beta

Also known as: FSGS10, LMX1.2, NPS1

This transcription factor is essential for normal development of dorsal limb structures, the glomerular basement membrane, the anterior eye segment, and dopaminergic and serotonergic neurons. Mutations cause nail-patella syndrome, an autosomal dominant disorder characterized by nail dysplasia, absent or hypoplastic patellae, elbow abnormalities, and nephropathy that can progress to chronic kidney disease. The gene shows moderate constraint against loss-of-function variants (LOEUF 0.415), consistent with its role in multiple developmental processes.

OMIMResearchSummary from RefSeq, UniProt
LOFmechanismADLOEUF 0.412 OMIM phenotypes
Clinical SummaryLMX1B
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Gene-Disease Validity (ClinGen)
nail-patella syndrome · ADDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.75) — some intolerance to loss-of-function variants.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.41LOEUF
pLI 0.746
Z-score 3.56
OE 0.18 (0.090.41)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
2.02Z-score
OE missense 0.65 (0.570.74)
169 obs / 260.8 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.18 (0.090.41)
00.351.4
Missense OE0.65 (0.570.74)
00.61.4
Synonymous OE1.10
01.21.6
LoF obs/exp: 4 / 22.1Missense obs/exp: 169 / 260.8Syn Z: -0.81
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
definitiveLMX1B-related nail-patella syndromeLOFAD
DN
0.5379th %ile
GOF
0.4480th %ile
LOF
0.68top 10%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · 1 literature citation · LOEUF 0.41

Literature Evidence

LOFLoss-of-function mutations in the LIM-homeodomain gene, LMX1B, in nail-patella syndromePMID:9618165

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

LMX1B · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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