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LIS1

Chr 17AD

platelet activating factor acetylhydrolase 1b regulatory subunit 1

Also known as: LIS1, LIS2, MDCR, MDS, NudF, PAFAH

This gene encodes the regulatory subunit of platelet-activating factor acetylhydrolase and is essential for dynein-mediated processes including neuronal migration during brain development. Mutations cause lissencephaly 1 and subcortical laminar heterotopia, cortical malformation disorders that typically present in infancy with seizures and developmental delays. Inheritance is autosomal dominant.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismAD2 OMIM phenotypes
Some data sources returned errors (2)

ensembl: Error: Ensembl fetch failed: 400 for https://rest.ensembl.org/lookup/symbol/homo_sapiens/LIS1?content-type=application/json&expand=1

gnomad: Error: Gene not found

Population Genetics & Constraint

Constraint data not available from gnomAD.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

LIS1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

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