LHX1

Chr 17

LIM homeobox 1

Also known as: LIM-1, LIM1

LHX1 encodes a LIM domain-containing transcription factor that is important for development of the renal and urogenital systems, as well as early mesoderm formation and neurogenesis. Mutations cause Mayer-Rokitansky-Kuster-Hauser syndrome, characterized by anomalies in the female genital tract. The gene shows low constraint against loss-of-function variants (pLI 0.03, LOEUF 0.74), and inheritance pattern information requires further clinical correlation.

GeneReviewsOMIMResearchSummary from RefSeq, UniProt
DNmechanismLOEUF 0.74
Clinical SummaryLHX1
Population Constraint (gnomAD)
Low constraint (pLI 0.03) — loss-of-function variants are relatively tolerated in the population.
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GeneReview available — LHX1
Authoritative clinical overview · Recommended first read
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Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.74LOEUF
pLI 0.029
Z-score 2.27
OE 0.35 (0.180.74)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
1.92Z-score
OE missense 0.64 (0.560.74)
146 obs / 227.6 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.35 (0.180.74)
00.351.4
Missense OE0.64 (0.560.74)
00.61.4
Synonymous OE1.24
01.21.6
LoF obs/exp: 5 / 14.3Missense obs/exp: 146 / 227.6Syn Z: -1.89
DN
0.7133th %ile
GOF
0.5464th %ile
LOF
0.4627th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

LHX1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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