The protein encoded by this gene is predicted to bind ATP, though its specific cellular function remains unclear. Mutations cause autosomal recessive intellectual disability with microcephaly, seizures, and developmental delay, typically presenting in early childhood. This gene is highly constrained against loss-of-function mutations, indicating it is essential for normal cellular function.

Summary from RefSeq
Research Assistant →
0
Active trials
0
Pubs (1 yr)
86
P/LP submissions
0%
P/LP missense
0.20
LOEUF· LoF intol.
LOF
Mechanism· predicted
Clinical SummaryKIAA0232
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
86 unique Pathogenic / Likely Pathogenic· 153 VUS of 268 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.20LOEUF
pLI 1.000
Z-score 6.17
OE 0.09 (0.050.20)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
1.20Z-score
OE missense 0.87 (0.820.93)
629 obs / 719.5 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.09 (0.050.20)
00.351.4
Missense OE0.87 (0.820.93)
00.61.4
Synonymous OE1.03
01.21.6
LoF obs/exp: 5 / 53.9Missense obs/exp: 629 / 719.5Syn Z: -0.40
DN
0.3495th %ile
GOF
0.4776th %ile
LOF
0.72top 10%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · LOEUF 0.20

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

268 submitted variants in ClinVar

Classification Summary

Pathogenic81
Likely Pathogenic5
VUS153
Likely Benign13
Benign5
Conflicting1
81
Pathogenic
5
Likely Pathogenic
153
VUS
13
Likely Benign
5
Benign
1
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
81
0
81
Likely Pathogenic
0
0
5
0
5
VUS
0
151
2
0
153
Likely Benign
0
10
0
3
13
Benign
0
3
0
2
5
Conflicting
1
Total0164885258

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

KIAA0232 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
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Key Publications
Landmark & review papers · by relevance
PubMed
Top 1 results · since 2015Search PubMed ↗
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found