JAK2

Chr 9ADSomatic

Janus kinase 2

Also known as: JTK10

This gene encodes a non-receptor tyrosine kinase that plays a central role in cytokine and growth factor signalling. The primary isoform of this protein has an N-terminal FERM domain that is required for erythropoietin receptor association, an SH2 domain that binds STAT transcription factors, a pseudokinase domain and a C-terminal tyrosine kinase domain. Cytokine binding induces autophosphorylation and activation of this kinase. This kinase then recruits and phosphorylates signal transducer and activator of transcription (STAT) proteins. Growth factors like TGF-beta 1 also induce phosphorylation and activation of this kinase and translocation of downstream STAT proteins to the nucleus where they influence gene transcription. Mutations in this gene are associated with numerous inflammatory diseases and malignancies. This gene is a downstream target of the pleiotropic cytokine IL6 that is produced by B cells, T cells, dendritic cells and macrophages to produce an immune response or inflammation. Disregulation of the IL6/JAK2/STAT3 signalling pathways produces increased cellular proliferation and myeloproliferative neoplasms of hematopoietic stem cells. A nonsynonymous mutation in the pseudokinase domain of this gene disrupts the domains inhibitory effect and results in constitutive tyrosine phosphorylation activity and hypersensitivity to cytokine signalling. This gene and the IL6/JAK2/STAT3 signalling pathway is a therapeutic target for the treatment of excessive inflammatory responses to viral infections. Alternative splicing results in multiple transcript variants encoding distinct isoforms. [provided by RefSeq, Jul 2020]

GeneReviewsOMIMResearchGenerating clinical summary…
MultiplemechanismAD/SomaticLOEUF 0.346 OMIM phenotypes
Clinical SummaryJAK2
Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.65) — some intolerance to loss-of-function variants.
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ClinVar Variants
2 unique Pathogenic / Likely Pathogenic· 241 VUS of 382 total submissions
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Clinical Trials
12 active or recruiting trials — potential therapeutic options may be available
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GeneReview available — JAK2
Authoritative clinical overview · Recommended first read
Open GeneReview ↗

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint?
0.34LOEUF
pLI 0.654
Z-score 5.66
OE 0.21 (0.140.34)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint?
0.90Z-score
OE missense 0.90 (0.830.96)
518 obs / 578.6 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios?
LoF OE?0.21 (0.140.34)
00.351.4
Missense OE?0.90 (0.830.96)
00.61.4
Synonymous OE?1.11
01.21.6
LoF obs/exp: 13 / 60.6Missense obs/exp: 518 / 578.6Syn Z: -1.21

This gene — mechanism propensity

DN
0.5575th %ile
GOF
0.6345th %ile
LOF
0.4628th %ile

This gene has evidence for multiple mechanisms of pathogenicity (gain-of-function and loss-of-function). Both the Badonyi & Marsh prediction and the broader genomic evidence point to gain-of-function as the predominant mechanism. Different variants in this gene may act through different mechanisms — interpret in context of the specific variant.

GOFprediction above median · 1 literature citation
LOFLOEUF 0.34

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Literature Evidence

GOFThrombotic complications are a major cause of death in patients with Philadelphia chromosome-negative myeloproliferative neoplasms (MPNs), which are closely associated with the JAK2 V617F activating mutation.1

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

References

  1. 1.PMID 24858412

ClinVar Variant Classifications

382 submitted variants in ClinVar

Classification Summary

Likely Pathogenic2
VUS241
Likely Benign112
Benign9
Conflicting1
2
Likely Pathogenic
241
VUS
112
Likely Benign
9
Benign
1
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
0
0
0
Likely Pathogenic
0
2
0
0
2
VUS
8
212
18
3
241
Likely Benign
1
4
42
65
112
Benign
0
0
7
2
9
Conflicting
1
Total92186770365

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

16 pathogenic / likely-pathogenic (of 18) ClinVar copy-number / structural variants overlap JAK2 — these span large chromosomal regions, not the gene specifically, and are excluded from the counts above. Explore in CNV tools →

Protein Context — Lollipop Plot

JAK2 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

T-cell LymphomaGraft Versus Host DiseaseLymphoma, T-Cell

Ruxolitinib Maintenance Post-Hematopoietic Stem Cell Transplant T-Cell Lymphoma

RECRUITING
NCT07356245Phase PHASE2Jonathan BrammerStarted 2026-02-12
RuxolitinibPositron emission tomography-computed tomographyBone Marrow Biopsy
Polycythemia VeraEssential ThrombocythaemiaMyelofibrosis

Prevalence Of Germline Gene Mutations In Patients With Myeloproliferative Neoplasms With Family History

NOT YET RECRUITING
NCT06923670Phase NAFondazione Policlinico Universitario Agostino Gemelli IRCCSStarted 2025-05-21
NGS testingNGS analysis for mutations in genes involved in familial predisposition to hematological malignancies
Giant Cell ArteritisTemporal ArteritisClonal Hematopoiesis of Indeterminate Potential

Clonal Hematopoiesis in Giant Cell Arteritis

NOT YET RECRUITING
NCT06244069ASST Fatebenefratelli SaccoStarted 2024-03
Temporal arterial biopsyWhole exome sequencingSingle cell transcriptomics
Myelofibrosis

Tasquinimod in Patients with Myelofibrosis Refractory to or Intolerant for JAK2 Inhibition

RECRUITING
NCT06605586Phase PHASE1, PHASE2Stichting Hemato-Oncologie voor Volwassenen NederlandStarted 2025-02-20
Tasquinimod
Acute Myeloid Leukemia (AML)

CART123 Cells With or Without Ruxolitinib in Relapsed/Refractory Acute Myeloid Leukemia

RECRUITING
NCT07464951Phase PHASE1Stephan Grupp MD PhDStarted 2026-05-14
Anti-CD123 LV redirected T cells (CART123)Ruxolitinib (JAKAVI®)
Myelofibrosis Transformation in Essential ThrombocythemiaPolycythemia Vera, Post-Polycythemic Myelofibrosis PhasePrimary Myelofibrosis

Elotuzumab for the Treatment of JAK2-Mutated Myelofibrosis

ACTIVE NOT RECRUITING
NCT04517851Phase PHASE2M.D. Anderson Cancer CenterStarted 2021-02-10
ElotuzumabQuestionnaire Administration
Chronic Myelomonocytic Leukemia

Relevance of Peripheral Cells in the Pathophysiology of Chronic Myelomonocytic Leukemia (CMML)

RECRUITING
NCT03280888Centre Hospitalier Universitaire de NiceStarted 2014-11-05
Aplastic AnemiaTPO Receptor Agonists

Standard Immunosuppressive Therapy Combined With Romiplostim N01 as First-line Treatment for Severe Aplastic Anemia

RECRUITING
NCT06613880Phase PHASE2Institute of Hematology & Blood Diseases Hospital, ChinaStarted 2024-10-24
standard IST combined with Romiplostim N01
Non-Small Cell Lung Cancer

Analysis of Drug Resistance in Immune Checkpoint Inhibitors of Non-small Cell Lung Cancer

RECRUITING
NCT04977791Shanghai Chest HospitalStarted 2016-07-21
Anti-PD-1/PD-L1 monoclonal antibody
Insulin ResistanceObesity & OverweightEnergy Metabolism

Effects of Ketone Bodies on Insulin Sensitivity

RECRUITING
NCT07359625Phase NAUniversity of AarhusStarted 2025-12-02
Growth Hormone, HumanOral ketone supplement (KetoAid®, KE4)Saline infusion (placebo)
Myelofibrosis

A Clinical Trial of TQ05105 Tablets Combined With TQB3617 Capsules in the Treatment of Myelofibrosis (MF)

RECRUITING
NCT06122831Phase PHASE1, PHASE2Chia Tai Tianqing Pharmaceutical Group Co., Ltd.Started 2023-12-12
TQ05105 TabletsTQB3617 Capsules
Myeloproliferative DiseaseGermline Mutation

Unveiling the Germline Predisposition to Myeloproliferative Neoplasms

RECRUITING
NCT07204392Fondazione IRCCS Policlinico San Matteo di PaviaStarted 2022-06-27