INTS8

Chr 8AR

integrator complex subunit 8

Also known as: C8orf52, INT8, NEDCHS

The INTS8 protein is a component of the integrator complex that terminates RNA polymerase II transcription and processes small nuclear RNAs, serving as a quality checkpoint during transcription elongation. Mutations cause an autosomal recessive neurodevelopmental disorder with cerebellar hypoplasia and spasticity. The gene is highly constrained against loss-of-function variants (pLI 0.94, LOEUF 0.31), indicating that functional copies are essential for normal development.

Summary from RefSeq, OMIM, UniProt
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Primary Disease Associations & Inheritance

?Neurodevelopmental disorder with cerebellar hypoplasia and spasticityMIM #618572
AR
0
Active trials
1
Pubs (1 yr)
42
P/LP submissions
2%
P/LP missense
0.31
LOEUF· LoF intol.
LOF
Mechanism· predicted
Clinical SummaryINTS8
Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 0.94). One damaged copy is likely sufficient to cause disease.
📋
ClinVar Variants
42 unique Pathogenic / Likely Pathogenic· 102 VUS of 223 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

LoF intolerant — likely haploinsufficient
LoF Constraint
0.31LOEUF
pLI 0.944
Z-score 5.89
OE 0.19 (0.120.31)
Highly constrained

Highly LoF-intolerant (top ~10% of genes)

Missense Constraint
2.03Z-score
OE missense 0.75 (0.690.81)
384 obs / 513.5 exp
Mild constraint

Moderately missense-constrained (top ~2.5%)

Observed / Expected Ratios
LoF OE0.19 (0.120.31)
00.351.4
Missense OE0.75 (0.690.81)
00.61.4
Synonymous OE1.01
01.21.6
LoF obs/exp: 12 / 62.0Missense obs/exp: 384 / 513.5Syn Z: -0.08
DN
0.2798th %ile
GOF
0.3292th %ile
LOF
0.72top 10%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · LOEUF 0.31

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

223 submitted variants in ClinVar

Classification Summary

Pathogenic39
Likely Pathogenic3
VUS102
Likely Benign14
Benign8
39
Pathogenic
3
Likely Pathogenic
102
VUS
14
Likely Benign
8
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
1
38
0
39
Likely Pathogenic
0
0
3
0
3
VUS
2
99
1
0
102
Likely Benign
0
7
0
7
14
Benign
0
0
5
3
8
Total21074710166

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

INTS8 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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