GNPTG

Chr 16AR

N-acetylglucosamine-1-phosphate transferase subunit gamma

Also known as: C16orf27, GNPTAG, LP2537, RJD9

The gamma subunit of N-acetylglucosamine-1-phosphotransferase enhances mannose 6-phosphate marker formation on lysosomal enzymes, which is essential for proper targeting of these enzymes to lysosomes. Mutations cause mucolipidosis III gamma, an autosomal recessive lysosomal storage disorder. This gene shows very low constraint against loss-of-function variants (pLI near zero), consistent with its recessive inheritance pattern.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismARLOEUF 1.221 OMIM phenotype
Clinical SummaryGNPTG
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Gene-Disease Validity (ClinGen)
GNPTG-mucolipidosis · ARDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.22LOEUF
pLI 0.000
Z-score 0.85
OE 0.79 (0.531.22)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
-2.06Z-score
OE missense 1.44 (1.301.60)
253 obs / 176.0 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.79 (0.531.22)
00.351.4
Missense OE1.44 (1.301.60)
00.61.4
Synonymous OE1.70
01.21.6
LoF obs/exp: 15 / 19.0Missense obs/exp: 253 / 176.0Syn Z: -4.86
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
definitiveGNPTG-related mucolipidosis type III complementation group CLOFAR

Predictions shown for reference only — model trained on dominant genes, not applicable to AR conditions.

DN
0.6452th %ile
GOF
0.4973th %ile
LOF
0.3068th %ile

The Badonyi & Marsh prediction model was trained exclusively on dominant disease genes. Predictions are not reliable for genes with autosomal recessive inheritance and are shown at reduced opacity for reference only.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

GNPTG · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC