GDF3

Chr 12

growth differentiation factor 3

Also known as: KFS3, MCOP7, MCOPCB6

This gene encodes a secreted ligand of the TGF-beta (transforming growth factor-beta) superfamily of proteins. Ligands of this family bind various TGF-beta receptors leading to recruitment and activation of SMAD family transcription factors that regulate gene expression. The encoded preproprotein is proteolytically processed to generate each subunit of the disulfide-linked homodimer. This protein plays a role ocular and skeletal development. Mutations in this gene are associated with microphthalmia, coloboma, and skeletal abnormalities in human patients. [provided by RefSeq, Aug 2016]

ResearchGenerating clinical summary…

Primary Disease Associations & Inheritance

UniProtKlippel-Feil syndrome 3, autosomal dominant
UniProtMicrophthalmia/Coloboma 6
UniProtMicrophthalmia, isolated, 7
0
Active trials
15
Pubs (1 yr)
P/LP submissions
P/LP missense
1.31
LOEUF
DN
Mechanism· predicted
Some data sources returned errors (1)

omim: Error: OMIM fetch failed: 429

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint?
1.31LOEUF
pLI 0.000
Z-score 0.84
OE 0.73 (0.431.31)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint?
-0.12Z-score
OE missense 1.02 (0.911.15)
202 obs / 197.4 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios?
LoF OE?0.73 (0.431.31)
00.351.4
Missense OE?1.02 (0.911.15)
00.61.4
Synonymous OE?0.99
01.21.6
LoF obs/exp: 8 / 11.0Missense obs/exp: 202 / 197.4Syn Z: 0.10

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

GDF3 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →