FGF20

Chr 8AR

fibroblast growth factor 20

Also known as: FGF-20, RHDA2

This gene encodes a secreted neurotrophic factor that regulates central nervous system development and function, with particular expression in the cerebellum. Mutations cause renal hypodysplasia/aplasia 2 through autosomal recessive inheritance. The gene shows high constraint against loss-of-function variants (pLI 0.81, LOEUF 0.54), suggesting intolerance to complete protein loss.

Summary from RefSeq, OMIM, UniProt
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Primary Disease Associations & Inheritance

?Renal hypodysplasia/aplasia 2MIM #615721
AR
0
Active trials
11
Pubs (1 yr)
0
P/LP submissions
P/LP missense
0.54
LOEUF
GOF
Mechanism· predicted
Clinical SummaryFGF20
Population Constraint (gnomAD)
Moderately constrained gene (pLI 0.81) — some intolerance to loss-of-function variants.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Moderate LoF intolerance
LoF Constraint
0.54LOEUF
pLI 0.814
Z-score 2.18
OE 0.00 (0.000.54)
Moderately constrained

More LoF-intolerant than ~75% of genes

Missense Constraint
-0.87Z-score
OE missense 1.25 (1.081.45)
121 obs / 96.8 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE0.00 (0.000.54)
00.351.4
Missense OE1.25 (1.081.45)
00.61.4
Synonymous OE1.30
01.21.6
LoF obs/exp: 0 / 5.6Missense obs/exp: 121 / 96.8Syn Z: -1.46
DN
0.5181th %ile
GOF
0.6930th %ile
LOF
0.54top 25%

The highest-scoring mechanism for this gene is gain-of-function.

GOFprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

FGF20 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Full-Text Mentions
NLP-detected gene mentions in article bodies · via PubTator3
PubTator3
Top 5 full-text resultsSearch PubTator3 ↗