FAM120B

Chr 6

family with sequence similarity 120 member B

Also known as: CCPG, KIAA1838, PGCC1, SAN1, dJ894D12.1

The protein functions as a transactivator of PPARG and ESR1, playing a role in adipogenesis through PPARG activation. Mutations cause neurodevelopmental disorders with intellectual disability and developmental delay, inherited in an autosomal dominant pattern. The gene is highly constrained against loss-of-function variants, indicating that such mutations are likely pathogenic.

OMIMResearchSummary from RefSeq, UniProt
DNmechanismLOEUF 0.75
Clinical SummaryFAM120B
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
84 unique Pathogenic / Likely Pathogenic· 103 VUS of 227 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.75LOEUF
pLI 0.000
Z-score 2.90
OE 0.53 (0.390.75)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.67Z-score
OE missense 0.91 (0.850.99)
453 obs / 495.2 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.53 (0.390.75)
00.351.4
Missense OE0.91 (0.850.99)
00.61.4
Synonymous OE1.08
01.21.6
LoF obs/exp: 24 / 45.0Missense obs/exp: 453 / 495.2Syn Z: -0.90
DN
0.6745th %ile
GOF
0.5268th %ile
LOF
0.3358th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

227 submitted variants in ClinVar

Classification Summary

Pathogenic77
Likely Pathogenic7
VUS103
Likely Benign14
Benign1
77
Pathogenic
7
Likely Pathogenic
103
VUS
14
Likely Benign
1
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
77
0
77
Likely Pathogenic
0
0
7
0
7
VUS
0
91
12
0
103
Likely Benign
0
12
0
2
14
Benign
0
0
1
0
1
Total0103972202

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

FAM120B · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
Open Research Assistant →
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC

No open access results found