EFR3A encodes a membrane-anchoring protein that localizes phosphatidylinositol 4-kinase to the plasma membrane and regulates phosphatidylinositol 4-phosphate synthesis, while also affecting G-protein-coupled receptor responsiveness. Mutations cause autism spectrum disorders with autosomal inheritance patterns. The gene is highly intolerant to loss-of-function variants, suggesting that even heterozygous mutations can cause disease.

Summary from RefSeq, UniProt
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0
Active trials
3
Pubs (1 yr)
0
P/LP submissions
P/LP missense
0.77
LOEUF
GOF
Mechanism· predicted
Clinical SummaryEFR3A
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.77LOEUF
pLI 0.000
Z-score 2.78
OE 0.55 (0.400.77)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.80Z-score
OE missense 0.89 (0.820.97)
376 obs / 422.0 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.55 (0.400.77)
00.351.4
Missense OE0.89 (0.820.97)
00.61.4
Synonymous OE1.02
01.21.6
LoF obs/exp: 24 / 43.9Missense obs/exp: 376 / 422.0Syn Z: -0.17
DN
0.6065th %ile
GOF
0.6833th %ile
LOF
0.3939th %ile

The highest-scoring mechanism for this gene is gain-of-function.

GOFprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

EFR3A · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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Clinical Literature
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Full-Text Mentions
NLP-detected gene mentions in article bodies · via PubTator3
PubTator3
Top 4 full-text resultsSearch PubTator3 ↗
Key Publications
Landmark & review papers · by relevance
PubMed
Top 2 results · since 2015Search PubMed ↗
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC