EFHC1

Chr 6

EF-hand domain containing 1

Also known as: EJM1, POC9, RIB72, dJ304B14.2

This gene encodes an EF-hand-containing calcium binding protein. The encoded protein likely plays a role in calcium homeostasis. Mutations in this gene have been associated with susceptibility to juvenile myoclonic epilepsy and juvenile absence epilepsy. Alternatively spliced transcript variants have been described. [provided by RefSeq, Feb 2010]

GeneReviewsResearchGenerating clinical summary…

Primary Disease Associations & Inheritance

UniProtJuvenile myoclonic epilepsy 1
UniProtJuvenile absence epilepsy 1

Clinical highlights

Gene-disease validity (ClinGen)
epilepsy · ADRefutedevidence has disproved this relationship
0
Active trials
4
Pubs (1 yr)
P/LP submissions
P/LP missense
1.21
LOEUF
Multiple*
Mechanism· predicted
📖
GeneReview available — EFHC1
Authoritative clinical overview · Recommended first read
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Some data sources returned errors (1)

omim: Error: OMIM fetch failed: 429

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint?
1.21LOEUF
pLI 0.000
Z-score 0.63
OE 0.88 (0.651.21)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint?
0.14Z-score
OE missense 0.98 (0.901.07)
350 obs / 357.5 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios?
LoF OE?0.88 (0.651.21)
00.351.4
Missense OE?0.98 (0.901.07)
00.61.4
Synonymous OE?0.95
01.21.6
LoF obs/exp: 28 / 31.8Missense obs/exp: 350 / 357.5Syn Z: 0.46

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

EFHC1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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