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DYT1

Chr 9AD

torsin family 1 member A

Also known as: AMC5, DQ2, DYT1

The protein functions as an AAA family ATPase with chaperone activity, controlling protein folding, synaptic vesicle recycling, and nuclear envelope integrity, with prominent expression in the substantia nigra. Mutations cause autosomal dominant torsion dystonia with early onset (childhood to young adulthood), primarily affecting movement through disruption of basal ganglia circuits. This is a well-characterized dystonia gene with established clinical guidelines available through GeneReviews.

OMIMResearchSummary from RefSeq, OMIM, UniProt
LOFmechanismAD1 OMIM phenotype
Some data sources returned errors (2)

ensembl: Error: Ensembl fetch failed: 400 for https://rest.ensembl.org/lookup/symbol/homo_sapiens/DYT1?content-type=application/json&expand=1

gnomad: Error: Gene not found

Population Genetics & Constraint

Constraint data not available from gnomAD.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

DYT1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

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Clinical Literature
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