DOORS

Chr 16AR

TBC1 domain family member 24

Also known as: DEE16, DFNA65, DFNB86, DOORS, EIEE16, EIM, EPRPDC, FIME

This gene encodes a TBC domain-containing protein that functions as a GTPase-activating protein for Rab small GTPases, which regulate membrane trafficking in cells. Mutations cause DOORS syndrome, a multisystem disorder affecting hearing, vision, skeletal development, and intellectual development. The condition follows autosomal recessive inheritance.

Summary from RefSeq, OMIM
Research Assistant →

Primary Disease Associations & Inheritance

DOORS syndromeMIM #220500
AR
7
Active trials
407
Pubs (1 yr)
0
P/LP submissions
P/LP missense
LOEUF
Mechanism
Clinical SummaryDOORS
💊
Clinical Trials
7 active or recruiting trials — potential therapeutic options may be available
📖
GeneReview available — DOORS
Authoritative clinical overview · Recommended first read
Open GeneReview ↗
Some data sources returned errors (2)

ensembl: Error: Ensembl fetch failed: 400 for https://rest.ensembl.org/lookup/symbol/homo_sapiens/DOORS?content-type=application/json&expand=1

gnomad: Error: Gene not found

Population Genetics & Constraint

Constraint data not available from gnomAD.

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

DOORS · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

IBMPFD

Natural History Study of Patients With VCP-related Disease

ACTIVE NOT RECRUITING
NCT04823143Nationwide Children's HospitalStarted 2021-03-18
Atypical Hemolytic Uremic Syndrome

Functional Implications of Rare Gene Mutations in aHUS Open the Door to Personalized Therapy

RECRUITING
NCT05805202Phase NAMario Negri Institute for Pharmacological ResearchStarted 2023-05-03
Blood sampling and urine analysis
Non-syndromic Retinitis Pigmentosa

Dose-escalation Study to Evaluate the Safety and Tolerability of GS030 in Subjects With Retinitis Pigmentosa

ACTIVE NOT RECRUITING
NCT03326336Phase PHASE1, PHASE2GenSight BiologicsStarted 2018-09-26
Gene therapy: GS030-DP AND Medical device: GS030-MD
Staphylococcus Aureus Bloodstream Infections (BSI; Bacteremia)

Linezolid Plus Standard of Care

RECRUITING
NCT06958835Phase NAUniversity Hospital, Basel, SwitzerlandStarted 2025-10-06
Linezolid 600 mgPlacebo
Blood Stream InfectionsVentilator Associated PneumoniaHealthcare Associated Infection

EaRly impAct theraPy With Ceftazidime-avibactam Via rapID Diagnostics

RECRUITING
NCT05979545Phase PHASE4National University of SingaporeStarted 2023-12-12
Rapid Diagnostics
Sexual Function AbnormalSpinal Cord Injuries (SCI)

A Prospective Cohort Study on the Effect of Spinal Spinal Cord Injury on Sexual Function in Male Patients

ACTIVE NOT RECRUITING
NCT07093827Peking University Third HospitalStarted 2020-01-01
Posterior decompression surgeryunilateral open-door laminoplastyPosterior lumbar discectomy with fusion
Cervical Spondylosis With Myelopathy

Cervical Spondylotic Myelopathy Surgical Trial

ACTIVE NOT RECRUITING
NCT02076113Phase NALahey ClinicStarted 2014-04-01
Ventral (Front) decompression with FusionDorsal (Back) Decompression with FusionDorsal (back) Laminoplasty
Clinical Literature
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Full-Text Mentions
NLP-detected gene mentions in article bodies · via PubTator3
PubTator3
The classroom door.
Croft C·Science
2025
Garage Door.
Davison NR·Am J Geriatr Psychiatry
2021
Top 5 full-text resultsSearch PubTator3 ↗