DNAAF5

Chr 7

dynein axonemal assembly factor 5

Also known as: CILD18, HEATR2

The protein encoded by this gene is essential for the preassembly or stability of axonemal dynein arms, and is found only in organisms with motile cilia and flagella. Mutations in this gene are associated with primary ciliary dyskinesia-18, a disorder characterized by abnormalities of motile cilia. Alternatively spliced transcript variants have been found for this gene. [provided by RefSeq, Feb 2013]

GeneReviewsResearchGenerating clinical summary…

Primary Disease Associations & Inheritance

UniProtCiliary dyskinesia, primary, 18

Clinical highlights

Gene-disease validity (ClinGen)
primary ciliary dyskinesia 18 · ARDefinitivesufficient evidence for diagnostic panels
0
Active trials
2
Pubs (1 yr)
P/LP submissions
P/LP missense
0.94
LOEUF
Mechanism
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GeneReview available — DNAAF5
Authoritative clinical overview · Recommended first read
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Some data sources returned errors (1)

omim: Error: OMIM fetch failed: 429

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint?
0.94LOEUF
pLI 0.000
Z-score 1.85
OE 0.65 (0.460.94)
Tolerant

Typical tolerance to LoF variation

Missense Constraint?
0.00Z-score
OE missense 1.00 (0.921.08)
440 obs / 440.1 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios?
LoF OE?0.65 (0.460.94)
00.351.4
Missense OE?1.00 (0.921.08)
00.61.4
Synonymous OE?1.12
01.21.6
LoF obs/exp: 21 / 32.3Missense obs/exp: 440 / 440.1Syn Z: -1.37

ClinVar Variant Classifications

0 submitted variants in ClinVar

Protein Context — Lollipop Plot

DNAAF5 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

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