DDX47

Chr 12

DEAD-box helicase 47

Also known as: E4-DBP, HQ0256, MSTP162, RRP3

The protein encoded by this gene is an RNA helicase that is required for efficient ribosome biogenesis and may function in mRNA splicing and apoptosis. Mutations cause autosomal recessive intellectual disability with language impairment and autistic features. This gene shows no constraint against loss-of-function variants based on population data.

Summary from RefSeq, UniProt
Research Assistant →
0
Active trials
0
Pubs (1 yr)
45
P/LP submissions
0%
P/LP missense
0.98
LOEUF
DN
Mechanism· predicted
Clinical SummaryDDX47
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
45 unique Pathogenic / Likely Pathogenic· 90 VUS of 158 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
0.98LOEUF
pLI 0.000
Z-score 1.63
OE 0.68 (0.470.98)
Tolerant

Typical tolerance to LoF variation

Missense Constraint
0.39Z-score
OE missense 0.93 (0.841.03)
250 obs / 268.2 exp
Tolerant

Mild missense constraint

Observed / Expected Ratios
LoF OE0.68 (0.470.98)
00.351.4
Missense OE0.93 (0.841.03)
00.61.4
Synonymous OE0.92
01.21.6
LoF obs/exp: 20 / 29.5Missense obs/exp: 250 / 268.2Syn Z: 0.62
DN
0.80top 25%
GOF
0.6150th %ile
LOF
0.2970th %ile

The highest-scoring mechanism for this gene is dominant-negative.

DNprediction above median

Note: In-silico variant effect predictors (SIFT, PolyPhen, REVEL, CADD) may underestimate pathogenicity of missense variants in genes with GOF or DN mechanisms. Consider functional evidence and clinical context.

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312.

ClinVar Variant Classifications

158 submitted variants in ClinVar

Classification Summary

Pathogenic43
Likely Pathogenic2
VUS90
Likely Benign1
43
Pathogenic
2
Likely Pathogenic
90
VUS
1
Likely Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
0
0
43
0
43
Likely Pathogenic
0
0
2
0
2
VUS
0
85
5
0
90
Likely Benign
0
0
1
0
1
Benign
0
0
0
0
0
Total085510136

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

DDX47 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →
Clinical Literature
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Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC