CSDE1

Chr 1

cold shock domain containing E1

Also known as: D1S155E, UNR

The CSDE1 protein is an RNA-binding protein that regulates mRNA stability and translation, and is required for stress granule formation during cellular stress. Mutations cause autosomal dominant neurodevelopmental disorders with intellectual disability, developmental delay, and variable features including seizures and behavioral abnormalities. This gene is highly constrained against loss-of-function variants in the population, indicating that such mutations are likely to be pathogenic.

Summary from RefSeq, UniProt
Research Assistant →
1
Active trials
16
Pubs (1 yr)
27
P/LP submissions
11%
P/LP missense
0.14
LOEUF· LoF intol.
LOF
Mechanism· G2P
Clinical SummaryCSDE1
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Gene-Disease Validity (ClinGen)
complex neurodevelopmental disorder · ADDefinitive

Definitive — sufficient evidence for diagnostic panels

Population Constraint (gnomAD)
Highly constrained gene — heterozygous loss-of-function variants are very rare in the population (pLI 1.00). One damaged copy is likely sufficient to cause disease.
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ClinVar Variants
27 unique Pathogenic / Likely Pathogenic· 131 VUS of 230 total submissions
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Clinical Trials
1 active or recruiting trial — potential therapeutic options may be available

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Dual constrained — LoF & missense intolerant
LoF Constraint
0.14LOEUF
pLI 1.000
Z-score 5.85
OE 0.05 (0.020.14)
Highly constrained

Among the most LoF-intolerant genes (~top 3%)

Missense Constraint
3.45Z-score
OE missense 0.55 (0.500.61)
259 obs / 469.5 exp
Constrained

Highly missense-constrained (top ~0.1%)

Observed / Expected Ratios
LoF OE0.05 (0.020.14)
00.351.4
Missense OE0.55 (0.500.61)
00.61.4
Synonymous OE0.96
01.21.6
LoF obs/exp: 2 / 43.8Missense obs/exp: 259 / 469.5Syn Z: 0.40
Curated Mechanism (G2P)Gene2Phenotype (DDG2P) ↗
limitedCSDE1-related intellectual disability and autismLOFAD
DN
0.3495th %ile
GOF
0.4381th %ile
LOF
0.82top 5%

The highest-scoring mechanism for this gene is loss-of-function (haploinsufficiency).

LOFprediction above median · 30% of P/LP variants are LoF · LOEUF 0.14

Predictions from Badonyi M, Marsh JA. PLoS ONE. 2024;19(8):e0307312. Mechanism ranking also informed by gnomAD constraint, ClinVar, and ClinGen data.

ClinVar Variant Classifications

230 submitted variants in ClinVar

Classification Summary

Pathogenic17
Likely Pathogenic10
VUS131
Likely Benign25
Benign6
17
Pathogenic
10
Likely Pathogenic
131
VUS
25
Likely Benign
6
Benign

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
5
0
12
0
17
Likely Pathogenic
3
3
4
0
10
VUS
5
114
12
0
131
Likely Benign
0
8
6
11
25
Benign
0
0
2
4
6
Total131253615189

LoF = frameshift, stop gained/lost, canonical splice · Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

CSDE1 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

3D Protein StructureAlphaFold
Clinical Literature
Open Research Assistant →
Full-Text Mentions
NLP-detected gene mentions in article bodies · via PubTator3
PubTator3
Top 5 full-text resultsSearch PubTator3 ↗
Recent Gene-Specific Literature
Gene in title · MEDLINE · newest first
Europe PMC