C4ORF50

Chr 4

chromosome 4 open reading frame 50

The protein encoded by this gene functions as a component of the mitochondrial ribosome, specifically involved in mitochondrial protein synthesis. Mutations cause autosomal recessive mitochondrial disorders including combined oxidative phosphorylation deficiency and Perrault syndrome, typically presenting with sensorineural hearing loss and neurological features. This gene shows low constraint against loss-of-function variants, consistent with its recessive inheritance pattern.

0
Active trials
1
Pubs (1 yr)
89
P/LP submissions
P/LP missense
1.45
LOEUF
Mechanism
Clinical SummaryC4ORF50
Population Constraint (gnomAD)
Low constraint (pLI 0.00) — loss-of-function variants are relatively tolerated in the population.
📋
ClinVar Variants
89 unique Pathogenic / Likely Pathogenic· 6 VUS of 101 total submissions

Population Genetics & Constraint

gnomAD v4 — loss-of-function & missense intolerance

Tolerant — LoF & missense variants common in population
LoF Constraint
1.45LOEUF
pLI 0.000
Z-score -0.25
OE 1.05 (0.781.45)
Tolerant

Highly tolerant — LoF variants common in population

Missense Constraint
-0.12Z-score
OE missense 1.02 (0.941.10)
422 obs / 414.9 exp
Tolerant

Tolerant to missense variation

Observed / Expected Ratios
LoF OE1.05 (0.781.45)
00.351.4
Missense OE1.02 (0.941.10)
00.61.4
Synonymous OE1.09
01.21.6
LoF obs/exp: 27 / 25.7Missense obs/exp: 422 / 414.9Syn Z: -0.98

ClinVar Variant Classifications

101 submitted variants in ClinVar

Classification Summary

Pathogenic84
Likely Pathogenic5
VUS6
Likely Benign4
Benign1
Conflicting1
84
Pathogenic
5
Likely Pathogenic
6
VUS
4
Likely Benign
1
Benign
1
Conflicting

Curated Variants Distribution

Classified variants from ClinVar · 5 ACMG categories· variant type breakdown unavailable

ClassificationLoFMissense + InframeNon-codingSynonymousTotal
Pathogenic
84
Likely Pathogenic
5
VUS
6
Likely Benign
4
Benign
1
Conflicting
1
Total101

Counts from ClinVar esearch · Updated hourly

View in ClinVar →

Protein Context — Lollipop Plot

C4ORF50 · protein map & ClinVar variants

Showing all ClinVar variants across the protein. Search a specific variant to highlight its position.

Clinical Trials

Active and recruiting trials from ClinicalTrials.gov

No active trials found for this gene.

Search ClinicalTrials.gov →